ABO-503
X-Linked Retinoschisis (XLRS)
- ABO-503 Current Phase
- Preclinical
ABO-504
Stargardt Disease
- ABO-504 Current Phase
- Preclinical
ABO-505
Autosomal Dominant Optic Atrophy (ADOA)
- ABO-505 Current Phase
- Preclinical
UX111*
Sanfilippo Syndrome Type A (MPS IIIA)
- UX111* Current Phase
- Phase 1/2
TSHA-102**
Rett Syndrome
- TSHA-102** Current Phase
- Phase 1/2
TSHA-118**
Infantile Batten Disease (CLN1 Disease)
- TSHA-118** Current Phase
- Phase 1/2
Partnered with *Ultragenyx Pharmaceutical Inc. **Taysha Gene Therapies, Inc.