Sanfilippo Syndrome Type A
(MPS IIIA)

Abeona Therapeutics Inc.

An open-label, dose-escalation clinical trial assessing the safety of one-time gene therapy ABO-102 for younger, higher-functioning patients with MPS IIIA.

View Study
Abeona Therapeutics Inc.

An open-label clinical trial assessing the safety of one-time gene therapy ABO-102 for patients with middle and advanced phases of MPS IIIA.

View Study